{"id":3888,"date":"2017-05-04T20:18:29","date_gmt":"2017-05-04T20:18:29","guid":{"rendered":"https:\/\/lpfch.org\/stanford-scientists-describe-stem-cell-and-gene-therapy-advances-in-scientific-symposium\/"},"modified":"2024-02-14T14:07:37","modified_gmt":"2024-02-14T14:07:37","slug":"stanford-scientists-describe-stem-cell-and-gene-therapy-advances-in-scientific-symposium","status":"publish","type":"post","link":"https:\/\/lpfch.org\/es\/impact-stories\/stanford-scientists-describe-stem-cell-and-gene-therapy-advances-in-scientific-symposium\/","title":{"rendered":"Cient\u00edficos de Stanford describen los avances en terapia g\u00e9nica y con c\u00e9lulas madre en un simposio cient\u00edfico."},"content":{"rendered":"<p>El uso de c\u00e9lulas madre y terapia g\u00e9nica para tratar o curar enfermedades a\u00fan puede sonar a ciencia ficci\u00f3n, pero una reciente reuni\u00f3n cient\u00edfica celebrada aqu\u00ed destac\u00f3 todos los frentes en los que se est\u00e1 acercando cada vez m\u00e1s a la realidad.<\/p>\n<p>\u201cEstamos entrando en una nueva era de la medicina\u201d, afirm\u00f3 Lloyd Minor, MD, decano de la Facultad de Medicina, en su discurso de apertura del primer simposio anual del nuevo Centro de Medicina Definitiva y Curativa de la facultad. Los investigadores de Stanford est\u00e1n preparados para utilizar c\u00e9lulas madre y terapia g\u00e9nica para mejorar una amplia gama de enfermedades, desde diagn\u00f3sticos comunes como la diabetes y el c\u00e1ncer hasta enfermedades raras del cerebro, la sangre, la piel, el sistema inmunitario y otros \u00f3rganos. En \u00faltima instancia, el objetivo es crear tratamientos \u00fanicos que puedan proporcionar curas de por vida; de ah\u00ed el t\u00e9rmino \u201cdefinitiva y curativa\u201d en el nombre del centro. Stanford es l\u00edder en esta rama de la investigaci\u00f3n m\u00e9dica, se\u00f1al\u00f3 Minor, y a\u00f1adi\u00f3: \u201cEste es un componente vital de nuestra visi\u00f3n de la medicina de precisi\u00f3n\u201d.<\/p>\n<p>Stanford cuenta con una larga trayectoria liderando descubrimientos de ciencia b\u00e1sica en biolog\u00eda de c\u00e9lulas madre, y actualmente se dedica a estudiar diversas maneras en que dichos descubrimientos podr\u00edan beneficiar a los pacientes, afirm\u00f3 la Dra. Maria Grazia Roncarolo, directora del nuevo centro. \u00abNuestro trabajo consiste en generar datos cl\u00ednicos tan convincentes que la industria adopte el producto y lo lleve a la siguiente fase\u00bb, declar\u00f3 Roncarolo ante el p\u00fablico.<\/p>\n<p>Entre otros aspectos destacados del evento:<\/p>\n<ul>\n<li>El oftalm\u00f3logo Jeffrey Goldberg, MD, PhD, inform\u00f3 que las t\u00e9cnicas con c\u00e9lulas madre pueden generar c\u00e9lulas de reemplazo para las da\u00f1adas en la capa interna de la c\u00f3rnea. Su equipo est\u00e1 llevando a cabo ensayos cl\u00ednicos iniciales con c\u00e9lulas corneales a las que se les ha adherido una nanopart\u00edcula magn\u00e9tica. Estas c\u00e9lulas magn\u00e9ticas se inyectan en el ojo y se mantienen en su lugar sobre la c\u00f3rnea mediante un parche ocular magn\u00e9tico. Los investigadores esperan que esta t\u00e9cnica pueda ayudar a algunos pacientes a evitar el trasplante de c\u00f3rnea.<\/li>\n<li>M\u00e1s personas podr\u00edan recibir trasplantes de m\u00e9dula \u00f3sea si el procedimiento no requiriera quimioterapia, explic\u00f3 la hemat\u00f3loga-onc\u00f3loga Judith Shizuru, MD, PhD, al p\u00fablico. En un ensayo cl\u00ednico recientemente iniciado, Shizuru y sus colegas est\u00e1n utilizando t\u00e9cnicas basadas en anticuerpos en lugar de quimioterapia para preparar a ni\u00f1os con inmunodeficiencia combinada grave (conocida como &quot;enfermedad del ni\u00f1o burbuja&quot;) para un trasplante de m\u00e9dula \u00f3sea.<\/li>\n<li>El Dr. Seung Kim describi\u00f3 c\u00f3mo las t\u00e9cnicas de investigaci\u00f3n con c\u00e9lulas madre facilitan la comprensi\u00f3n de la posible generaci\u00f3n de nuevas c\u00e9lulas beta pancre\u00e1ticas para personas con diabetes tipo 1. En relaci\u00f3n con esto, su colega, el Dr. Hiromitsu Nakauchi, demostr\u00f3 recientemente que se pueden cultivar p\u00e1ncreas de rat\u00f3n en ratas y utilizarlos para tratar la diabetes en ratones.<\/li>\n<li>Aunque la anemia falciforme ahora se puede tratar con trasplantes de m\u00e9dula \u00f3sea, muchos pacientes carecen de un donante compatible, afirm\u00f3 el Dr. Matthew Porteus, cuya foto aparece arriba. Su laboratorio est\u00e1 estudiando c\u00f3mo las t\u00e9cnicas de edici\u00f3n gen\u00e9tica (incluida la CRISPR) podr\u00edan permitir a los cient\u00edficos corregir el error gen\u00e9tico subyacente directamente en el cuerpo del paciente.<\/li>\n<li>Expertos en inmunoterapia contra el c\u00e1ncer, como la Dra. Crystal Mackall, se esfuerzan por crear nuevos tratamientos que el c\u00e1ncer no pueda burlar. \u00abHist\u00f3ricamente, atac\u00e1bamos los tumores con venenos o agentes dirigidos\u00bb, explic\u00f3 Mackall. \u00abLo que ha cambiado es que ahora tambi\u00e9n podemos atacar al hu\u00e9sped y modificar su respuesta al tumor\u00bb. Su equipo est\u00e1 modificando c\u00e9lulas T, un tipo de c\u00e9lula inmunitaria, para estimular al organismo del paciente a atacar tumores que han dejado de responder a la quimioterapia tradicional. Su trabajo a\u00fan no ha alcanzado el \u00e9xito deseado: algunas c\u00e9lulas tumorales logran evadir las c\u00e9lulas T y volver a crecer. Sin embargo, Mackall se muestra optimista. \u00abEstamos al final del principio\u00bb, afirm\u00f3.<\/li>\n<\/ul>\n<p>Encontrar\u00e1 m\u00e1s informaci\u00f3n sobre los acontecimientos del d\u00eda en <a href=\"http:\/\/www.mercurynews.com\/2017\/02\/07\/stanford-team-is-growing-healthy-skin-for-diseased-patients\/\" target=\"_blank\" rel=\"noopener\">Un art\u00edculo del San Jose Mercury News<\/a> Eso describe c\u00f3mo el Dr. Anthony Oro y sus colegas luchan contra la epiderm\u00f3lisis bullosa, una devastadora enfermedad gen\u00e9tica de la piel. Oro cerr\u00f3 su charla con una foto un tanto c\u00f3mica de un hombre bronce\u00e1ndose con spray. Caus\u00f3 risas, pero su argumento era serio: \u00abNuestro objetivo para la terapia celular del futuro es aplicar piel artificial mediante spray para corregir una terrible enfermedad gen\u00e9tica\u00bb.<\/p>\n<p>\u00bfAmbicioso? S\u00ed. \u00bfCiencia ficci\u00f3n? En el futuro, tal vez no.<\/p>\n<p><em>Esta historia apareci\u00f3 originalmente en <a href=\"http:\/\/scopeblog.stanford.edu\/2017\/02\/09\/stanford-scientists-describe-stem-cell-and-gene-therapy-advances-in-scientific-symposium\/\" target=\"_blank\" rel=\"noopener\">ALCANCE<\/a>.<\/em><\/p>","protected":false},"excerpt":{"rendered":"<p>El uso de c\u00e9lulas madre y terapia gen\u00e9tica para tratar o curar enfermedades todav\u00eda puede parecer ciencia ficci\u00f3n, pero una reuni\u00f3n cient\u00edfica reciente aqu\u00ed enfatiz\u00f3\u2026<\/p>","protected":false},"author":17,"featured_media":14834,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"_relevanssi_hide_post":"","_relevanssi_hide_content":"","_relevanssi_pin_for_all":"","_relevanssi_pin_keywords":"","_relevanssi_unpin_keywords":"","_relevanssi_related_keywords":"","_relevanssi_related_include_ids":"","_relevanssi_related_exclude_ids":"","_relevanssi_related_no_append":"","_relevanssi_related_not_related":"","_relevanssi_related_posts":"","_relevanssi_noindex_reason":"","footnotes":""},"categories":[148],"class_list":["post-3888","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-in-the-news"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO Premium plugin v27.2 (Yoast SEO v27.2) - 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